DMD Main

Sarepta Therapeutics has followed through on its promise to file for accelerated approval of its gene therapy SRP-9001

Sarepta files Duchenne muscular dystrophy gene therapy with FDA

https://pharmaphorum.com/news/sarepta-files-duchenne-muscular-dystrophy-gene-therapy-with-fda/

Disease Spotlight/ DMD Main/ Views and analysis

Curing DMD: Travelling together to find a meaningful destination

Amanda Barrell disease, DMD, Duchenne muscular dystrophy, Duchenne Parent Project Spain, Joaquim Brites, Marisol Montolio 0 Comment

For many years, Duchenne muscular dystrophy (DMD) was something of a forgotten disease. The boys, and some girls,

Curing DMD: Travelling together to find a meaningful destination

https://pharmaphorum.com/disease-spotlight/dmd-main/curing-dmd-travelling-together-to-find-a-meaningful-destination/

Growing concept eco Group hand children planting together on soil backgroud

Disease Spotlight/ DMD Main/ Views and analysis

Increase collaboration to widen access to DMD drugs, trials and care

louise.bellamy@pharmaphorum.com access to clinical trials, access to drugs, DMD, Duchenne muscular dystrophy 0 Comment

When it comes to fighting a rare disease like Duchenne muscular dystrophy (DMD), it’s a matter of strength

Increase collaboration to widen access to DMD drugs, trials and care

https://pharmaphorum.com/disease-spotlight/increase-collaboration-to-widen-access-to-dmd-drugs-trials-and-care/

Disease Spotlight/ DMD Main/ Views and analysis

DMD campaigners: Advocating for change

Dominic Tyer disease, DMD, DMD campaigners, DMD campaigning, Duchenne, Klair Bayley, Parent Project Muscular Dystrophy, Pat Furlong, Ricky Andreis, Santhera, Save Our Sons, Swedish Muscular Dystrophy Research Foundation 0 Comment

The internet and social media are often heralded as a panacea for rare disease patients and their carers

DMD campaigners: Advocating for change

https://pharmaphorum.com/disease-spotlight/dmd-main/dmd-campaigners-advocating-change/

Disease Spotlight/ DMD Main/ Views & Analysis

Parenting as a DMD patient

Dominic Tyer DMD, Duchenne muscular dystrophy, Mitch Coles, Muscular Dystrophy UK, Trailblazers 0 Comment

Parenting as a DMD patient The sleepless nights and steep learning curve that will be familiar to any

Parenting as a DMD patient

https://pharmaphorum.com/views-analysis-digital/parenting-as-a-dmd-patient/

Hands were a collaboration concept of teamwork

Disease Spotlight/ DMD Main/ Views and analysis

He ain’t heavy – learning about a sibling’s DMD diagnosis

Dominic Tyer DMD, DMD diagnosis, Duchenne muscular dystrophy, patient centricity, rare disease 0 Comment

It’s common for patients to want to know more about what’s causing them to be ill and their

He ain’t heavy – learning about a sibling’s DMD diagnosis

https://pharmaphorum.com/views-and-analysis/learning-sibling-dmd-diagnosis/

Group of people holding hand together in the park

Disease Spotlight/ DMD Main/ eyeforpharma Barcelona 2015/ Patients/ Views and analysis

Living with DMD: Ensuring equal access to quality of life

Linda Banks DMD, Duchenne muscular dystrophy, patient perspective, patient voice, patients 0 Comment

Making sure everyone with DMD gets access to treatments and the ‘essential’ interventions that can make life worth living is key.

Living with DMD: Ensuring equal access to quality of life

https://pharmaphorum.com/views-and-analysis/living-with-dmd-ensuring-equal-access-to-quality-of-life/

Disease Spotlight/ DMD Main/ Patients/ Views and analysis

Lights, camera, action – DMD and chasing your dreams

Linda Banks DMD, Duchenne muscular dystrophy, patient perspective, patient voice 0 Comment

People with a DMD diagnosis must believe this isn’t a sign to roll the end credits on their

Lights, camera, action – DMD and chasing your dreams

https://pharmaphorum.com/views-and-analysis/lights-camera-action-dmd-and-chasing-your-dreams/

Disease Spotlight/ DMD Main/ Patients/ Views and analysis

Living with DMD: Inspiring each other’s futures

Linda Banks DMD, Duchenne, Duchenne muscular dystrophy, patient group, patient organisation 0 Comment

Diagnosed with Duchenne muscular dystrophy (DMD) at three years old, Dr Jon Hastie grew up never thinking about

Living with DMD: Inspiring each other’s futures

https://pharmaphorum.com/views-and-analysis/living-with-dmd-inspiring-each-others-futures/

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